Gene-based medicines
At CRISPR Therapeutics, we are focused on developing transformative gene-based medicines for serious human diseases
We are rapidly translating our specific, efficient and versatile CRISPR/Cas9 gene-editing platform into therapies to treat hemoglobinopathies, cancer, diabetes and other diseases
Our multi-disciplinary team of world-class researchers and drug developers works every day to translate our CRISPR/Cas9 technology into breakthrough human therapeutics. Our lead program targeting the blood diseases β-thalassemia and sickle cell disease has entered clinical testing, as has our first allogeneic CAR-T program targeting B-cell malignancies. We are also advancing additional blood stem cell, immuno-oncology, regenerative medicine and in vivo programs towards the clinic.
Your request has been submitted successfully.
Knowledge
-
THE HUMAN FUTURE: A Case for Optimism
[embed]https://youtu.be/o48X3_XQ9to[/embed].
-
Meta Just Launched the Largest ‘Openâ€
In the world of artificial intelligence, a b.
-
This Is What Could Happen if AI Content
Generative AI is a data hog. The algorithms .
-
AI-Powered Weather and Climate Models Ar
A new system for forecasting weather and pred.
